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Dernières publications
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Francesco Galli, Laricia Bragg, Maira Rossi, Daisy Proietti, Laura Perani, et al.. Cell-mediated exon skipping normalizes dystrophin expression and muscle function in a new mouse model of Duchenne Muscular Dystrophy. EMBO Molecular Medicine, 2024, 16 (4), pp.927 - 944. ⟨10.1038/s44321-024-00031-3⟩. ⟨hal-04603972⟩
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Ekaterina Kiseleva, Olesya Serbina, Anna Karpukhina, Vincent Mouly, Yegor S Vassetzky. Interaction between mesenchymal stem cells and myoblasts in the context of facioscapulohumeral muscular dystrophy contributes to the disease phenotype. Journal of Cellular Physiology, 2022, 237 (8), pp.3328-3337. ⟨10.1002/jcp.30789⟩. ⟨hal-03796151⟩
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Muhammad Haseeb Iqbal, Jeanne Rosine Faratiana, Emeline Pradel, Varvara Gribova, Kamel Mamchaoui, et al.. Brush-Induced Orientation of Collagen Fibers in Layer-by-Layer Nanofilms: A Simple Method for the Development of Human Muscle Fibers. ACS Nano, In press, ⟨10.1021/acsnano.2c06329⟩. ⟨hal-03832239⟩
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Elena Marchesi, Matteo Bovolenta, Lorenzo Preti, Massimo L Capobianco, Kamel Mamchaoui, et al.. Synthesis and Exon-Skipping Properties of a 3′-Ursodeoxycholic Acid-Conjugated Oligonucleotide Targeting DMD Pre-mRNA: Pre-Synthetic versus Post-Synthetic Approach. Molecules, 2021, 26 (24), pp.7662. ⟨10.3390/molecules26247662⟩. ⟨hal-03510261⟩
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Manuel Schmidt, Anja Weidemann, Christine Poser, Anne Bigot, Julia von Maltzahn. Stimulation of Non-canonical NF-κB Through Lymphotoxin-β-Receptor Impairs Myogenic Differentiation and Regeneration of Skeletal Muscle. Frontiers in Cell and Developmental Biology, 2021, 9, ⟨10.3389/fcell.2021.721543⟩. ⟨hal-03405959⟩
Chiffres clés
48
Publications avec texte intégral
Open Access
87 %
Mots clés
Human
Gene therapy
Bile acid
Lamin A/C nuclei
DNM2
Cell Therapy
Human artificial chromosomes
Duchenne Muscular Dystrophy
MT RNA/DNA Editing
CDNA synthesis
Motor neuron
FoxO
Neuromuscular junction
Glucose
DMD
Duchenne muscular dystrophy
Dynamin 2
Gel electrophoresis
3D co-culture
DM1 myoblasts
Antisense oligonucleotide
CXCL12
Flavonoid
Migration
Myotube
Mdx
CLS
LTβR
Immortalized dystrophic canine myoblast
Autophagosome
Eteplirsen
Actin
Exon Skipping
LRP4
Cell biology
Adhesion
Machine learning
Insulin
Antisense morpholino
Exon skipping
DsDNA break repair
Expanded repeats
Drisapersen
Computer software
BAF
Fear response
Endocytosis
Canine X-linked muscular dystrophy in Japan CXMD J
Dominant centronuclear myopathy
Fibrosis
Exon-skipping
ICU-acquired weakness
CXCR4
Acetylcholine receptor subunit epsilon
Centronuclear myopathy
MSCs
Adeno-associated viral vector
Gut microbiota
Allele-specific silencing
Allele-specific silencing therapy
Gene Therapy
Laminographie
Dystrophin
FSHD
Fibroblast
Chromatin
Skeletal muscle
Myotonic dystrophy
Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS
Differentiation
CMS
ITSN1
Lymphotoxin-β-receptor
Cell-penetrating peptide
CRISPR/Cas9
Emerin
Clinical trial candidate screening
CFTR correctors
Muscle
Conjugation
CTG⋅CAGn repeat
Folding-defective proteins
Immortalisation
Human muscle stem/progenitor cells
HDMD/Dmd-null mice
Lamina-associated domain
Becker muscular dystrophy
Gene network analysis
Glucocorticoid-induced muscle atrophy
Exondys 51
Developmental biology
Autophagy
BMD
Coculture
DiPRO1
RNA interference
Myogenesis
KLF15
Alternative splicing
Atrial cardiac defects